Questions and Answers
What is the main goal of gene therapy?
To treat loss-of-function genetic disorders by delivering correcting therapeutic DNA sequences into the nucleus of a cell
What is the division of gene therapy that aims for the introduction of therapeutic genes into germ-cells or specific type of embryonal cells?
Germ-line gene therapy
Which type of gene therapy allows genetic manipulation of a patient’s somatic cells for the purpose of correcting severe disorders?
Somatic gene therapy
What are the principles of gene therapy?
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What is a major limitation of gene therapy, related to the nature of cells?
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What was the first disease target for gene therapy?
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What is the first gene therapy product known as Gendicine designed to treat?
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What is the gene therapy approach for treating Cystic Fibrosis?
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What is a characteristic of suicide gene therapy for cancer?
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What is the major concern about using viral vectors in gene therapy?
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"Hard to rapidly integrate therapeutic DNA into genome" is a limitation of gene therapy due to:
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What is the main challenge in treating multigene disorders with gene therapy?
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"New things introduced into the body leads to immune response" is a limitation related to:
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"The first gene therapy was performed on September 14th, 1990" was targeted at treating which condition?
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"Gendicine is a recombinant adenovirus engineered to express wildtype-p53" is designed for treating:
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