Podcast
Questions and Answers
What is the main goal of gene therapy?
What is the main goal of gene therapy?
What is the division of gene therapy that aims for the introduction of therapeutic genes into germ-cells or specific type of embryonal cells?
What is the division of gene therapy that aims for the introduction of therapeutic genes into germ-cells or specific type of embryonal cells?
Which type of gene therapy allows genetic manipulation of a patient’s somatic cells for the purpose of correcting severe disorders?
Which type of gene therapy allows genetic manipulation of a patient’s somatic cells for the purpose of correcting severe disorders?
What are the principles of gene therapy?
What are the principles of gene therapy?
Signup and view all the answers
What is a major limitation of gene therapy, related to the nature of cells?
What is a major limitation of gene therapy, related to the nature of cells?
Signup and view all the answers
What was the first disease target for gene therapy?
What was the first disease target for gene therapy?
Signup and view all the answers
What is the first gene therapy product known as Gendicine designed to treat?
What is the first gene therapy product known as Gendicine designed to treat?
Signup and view all the answers
What is the gene therapy approach for treating Cystic Fibrosis?
What is the gene therapy approach for treating Cystic Fibrosis?
Signup and view all the answers
What is a characteristic of suicide gene therapy for cancer?
What is a characteristic of suicide gene therapy for cancer?
Signup and view all the answers
What is the major concern about using viral vectors in gene therapy?
What is the major concern about using viral vectors in gene therapy?
Signup and view all the answers
"Hard to rapidly integrate therapeutic DNA into genome" is a limitation of gene therapy due to:
"Hard to rapidly integrate therapeutic DNA into genome" is a limitation of gene therapy due to:
Signup and view all the answers
What is the main challenge in treating multigene disorders with gene therapy?
What is the main challenge in treating multigene disorders with gene therapy?
Signup and view all the answers
"New things introduced into the body leads to immune response" is a limitation related to:
"New things introduced into the body leads to immune response" is a limitation related to:
Signup and view all the answers
"The first gene therapy was performed on September 14th, 1990" was targeted at treating which condition?
"The first gene therapy was performed on September 14th, 1990" was targeted at treating which condition?
Signup and view all the answers
"Gendicine is a recombinant adenovirus engineered to express wildtype-p53" is designed for treating:
"Gendicine is a recombinant adenovirus engineered to express wildtype-p53" is designed for treating:
Signup and view all the answers
