Podcast
Questions and Answers
Which technique can be used to correct and add genes in patient-derived stem cells or somatic cells?
Which technique can be used to correct and add genes in patient-derived stem cells or somatic cells?
- RNA-targeting
- CRISPR/Cas9 (correct)
- Dystrophic epidermolysis bullosa
- Down syndrome
Which diseases have genetic correction been achieved in cultured human cells derived from patients?
Which diseases have genetic correction been achieved in cultured human cells derived from patients?
- Duchenne muscular dystrophy, Down syndrome, chronic granulomatous disease
- Hepatitis C virus, cystic fibrosis, sickle cell disease
- Sickle cell disease, chronic granulomatous disease, Down syndrome
- Recessive dystrophic epidermolysis bullosa, Duchenne muscular dystrophy, cystic fibrosis (correct)
Which endonuclease is capable of targeting endogenous bacterial RNA?
Which endonuclease is capable of targeting endogenous bacterial RNA?
- FnCas9 (correct)
- CRISPR
- Dystrophic epidermolysis bullosa
- Down syndrome
What can FnCas9 be directed by to target and inhibit a human +ssRNA virus?
What can FnCas9 be directed by to target and inhibit a human +ssRNA virus?
Which virus can be targeted and inhibited by FnCas9 within eukaryotic cells?
Which virus can be targeted and inhibited by FnCas9 within eukaryotic cells?