5 Questions
Which technique can be used to correct and add genes in patient-derived stem cells or somatic cells?
CRISPR/Cas9
Which diseases have genetic correction been achieved in cultured human cells derived from patients?
Recessive dystrophic epidermolysis bullosa, Duchenne muscular dystrophy, cystic fibrosis
Which endonuclease is capable of targeting endogenous bacterial RNA?
FnCas9
What can FnCas9 be directed by to target and inhibit a human +ssRNA virus?
Engineered RNA-targeting guide RNA
Which virus can be targeted and inhibited by FnCas9 within eukaryotic cells?
Hepatitis C virus
Test your knowledge on gene correction and addition in patient-derived pluripotent stem cells/somatic cells using CRISPR/Cas9. Explore the potential therapeutic opportunities for diverse genetic and acquired diseases. Learn about successful genetic correction achieved in cultured human cells derived from patients with diseases like recessive dystrophic epidermolysis bullosa and Duchenne muscular dystrophy.
Make Your Own Quizzes and Flashcards
Convert your notes into interactive study material.
Get started for free
