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U7snRNA-Based Exon Skipping in HCM Mouse Model

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Questions and Answers

What is the purpose of the Terms and Conditions on Wiley Online Library?

To outline the production of adeno-associated virus vectors
To govern the use of OA articles under the Creative Commons License (correct)
To describe the use of morpholino antisense oligonucleotides
To provide rules for Duchenne muscular dystrophy research

What is the main topic of the 2012 study by Goyenvalle et al.?

Production of adeno-associated virus vectors
Exon skipping for Duchenne muscular dystrophy (correct)
Neonatal gene therapy using AAV-based vectors
Gene therapy for hemophilia A

What is the purpose of the study by Heemskerk et al. in 2009?

To develop a new method for Duchenne muscular dystrophy treatment
To study the use of RNA-targeting approaches for neuromuscular diseases
To compare AAV vectors for gene therapy
To compare 2'-O-methyl phosphorothioate and morpholino antisense oligonucleotides for exon skipping (correct)

What is the title of the 2006 study by Inagaki et al.?

Robust systemic transduction with AAV vectors in mice (D) Signup and view all the answers

What is the main topic of the 2003 study by Grimm et al.?

Production of adeno-associated virus vectors of serotypes 1 to 6 (C) Signup and view all the answers

What is the title of the 2012 study by Hu and Lipshutz?

AAV-based neonatal gene therapy for hemophilia A (D) Signup and view all the answers

What is the topic of the study by Le Roy et al. in 2009?

RNA-targeting approaches for neuromuscular diseases (C) Signup and view all the answers

What is the purpose of AAV vectors in the study by Inagaki et al.?

To achieve robust systemic transduction in mice (B) Signup and view all the answers

What is the topic of the study by Heemskerk et al. in 2009?

In vivo comparison of 2'-O-methyl phosphorothioate and morpholino antisense oligonucleotides (B) Signup and view all the answers

What is the main topic of the study by Goyenvalle et al. in 2012?

Engineering multiple U7snRNA constructs to induce single and multi-exon skipping (A) Signup and view all the answers

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